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Avrobio receives FDA rare pediatric disease status for cystinosis therapy

Pharmaceutical Technology

Avrobio has received rare pediatric disease designation from the US Food and Drug Administration (FDA) for its investigational gene therapy, AVR-RD-04, designed to treat cystinosis. AVR-RD-04 works by genetically modify a patient's hematopoietic stem cells (HSCs) to express the gene that encodes the cystinosin protein.

FDA 59
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The best diet for acne

The Checkup by Singlecare

RD, a senior clinical dietitian at UCLA medical center and author of Recipe for Survival. It has also been shown in some earlier clinical trials that some people with acne had zinc deficiency, and when treated with zinc supplements, they saw an improvement in their condition.

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Thyroid Antibodies Part 2: Mechanisms to Reduce Thyroid Antibodies

The Thyroid Pharmacist

After the nine-month trial, there was a significant decrease in serum TSH and TPO antibodies (a 54 percent reduction!), 32] During the trial, serum thyroid stimulating hormone (TSH) levels reduced from an average of 6.42 A dosage of 200 mcg per day has been found to reduce thyroid antibodies in clinical trials. [41]

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How Does Carnitine Support Hashimoto’s?

The Thyroid Pharmacist

In clinical studies, many patients with ASD have increased levels of propionic acid in the stool, as well as a history of previous infections; many also have carnitine deficiency. Clinical trials have shown that some carnitine forms, such as ALCAR, reduce pain and vascular-related symptoms in diabetic patients as well. (5).