Remove tag b-cell-biology
article thumbnail

CSL doses first patient with haemophilia B gene therapy Hemgenix

Pharmaceutical Technology

CSL announced the first patient with haemophilia B has been treated with its recently approved gene therapy Hemgenix (etranacogene dezaparvovec). Hemgenix is the first and only gene therapy approved for haemophilia B. This followed positive results from CSL’s Phase III HOPE-B trial (NCT03569891).

FDA 98
article thumbnail

Putting complex medicines under the microscope

European Pharmaceutical Review

Advanced light microscopy techniques have emerged as a foundation of biomedical research, capable of visualising cellular functions at very high resolution whilst being minimally invasive to the cells or tissues of interest. Dr Lorna Fitzpatrick is Lead Scientist – Cell and Molecular Engineering, Medicines Discovery Catapult.

Insiders

Sign Up for our Newsletter

This site is protected by reCAPTCHA and the Google Privacy Policy and Terms of Service apply.

Trending Sources

article thumbnail

Developing point-of-care CAR T manufacturing

European Pharmaceutical Review

Chimeric antigen receptor (CAR) T cells are the first example of a “living drug”. 1 Following in vitro production from T cells collected from a patient’s leukapheresis procedure, the CAR T cells are infused back into the patient’s blood, where they proliferate and expand. This is variable and to some extent unpredictable.

article thumbnail

Osteopathic Medicine and Surviving Your Second Year of Medical School with Dr. Bryce Brohol ?

The Physician Pharmacist

you know, taking general science courses or four years, we were taking pharmaceutics and all these, these clinical body system pharmaceutical courses with high level biology, chemistry, so in they don't really give you a lot too much slack. So I don't know why we have to look at, you know, cells in a petri dish. O l@liberty.edu.