Sun.Jul 16, 2023

article thumbnail

Researchers turn to CRISPR to unlock one of the trickiest diseases to treat: Alzheimer’s

STAT

When the genome-editing tool CRISPR is thought of as a potential medicine, the targets that first come to mind are diseases like sickle cell or other conditions caused by particular mutations. Use CRISPR to fix that mutation, the idea goes, and you can treat the disease. But a pair of abstracts being presented Sunday at a medical conference highlight how, just a decade after CRISPR’s debut, researchers are deploying the tool at diseases with more complicated roots that go beyond genetics.

98
article thumbnail

First Wave faces choppy waters with cystic fibrosis drug

pharmaphorum

First Wave faces choppy waters with cystic fibrosis drug Phil.

98
Insiders

Sign Up for our Newsletter

This site is protected by reCAPTCHA and the Google Privacy Policy and Terms of Service apply.

Trending Sources

article thumbnail

STAT+: Argenx antibody drug significantly slows progression of nerve disorder that robs patients of muscle strength

STAT

Belgian drugmaker Argenx said Monday that its antibody treatment called Vyvgart significantly delayed the progression of an autoimmune nerve disorder that causes people to lose feeling and muscle strength in the arms and legs. The positive outcome — a 61% reduction in the risk of relapse compared to a placebo — achieved the main goal of a Phase 3 clinical trial designed to demonstrate Vyvgart’s benefit for patients with chronic inflammatory demyelinating polyneuropathy, or C

FDA 97
article thumbnail

Lilly bulks up in obesity with $1.93bn Versanis buy

pharmaphorum

Lilly bulks up in obesity with $1.93bn Versanis buy Phil.

94
article thumbnail

Position Your Pharmacy for Expansion

Speaker: Chris Antypas and Josh Halladay

Access to limited distribution drugs and payer contracts are key to pharmacy expansion. But how do you prepare your operations to take the next step? Meaningful data: Collect and share clinical data regarding outcomes, utilization, and more Reporting: Limited distribution models require efficient tracking and reporting systems Workflows: Align workflows with specific pharma and payer contractual requirements For in-depth, expert insights on pharmacy expansion, watch this webinar from Inovalon.

article thumbnail

Should SPS (Kayexalate) Ever Be Used?

Med Ed 101

Sodium polystyrene sulfonate (SPS, Kayexalate) has been used for decades to help lower potassium levels and manage hyperkalemia. It does this by exchanging sodium ions for potassium ions in the gut (primarily the large intestine). The compound is then removed from the body out through the stool. It has some risks and controversy associated with […] The post Should SPS (Kayexalate) Ever Be Used?

article thumbnail

Boost Productivity and Eliminate Waste in Raw Material ID

BioPharm

Webinar Date/Time: Thu, Aug 17, 2023 11:00 AM EDT

52
article thumbnail

CancerX: Reducing Burden and Disparities in Cancer Care

PharmExec

Webinar Date/Time: Thu, Aug 17, 2023 10:00 AM EDT

52