Pharmaceutical Technology

MAY 2, 2023

Despite the significant advances that have been made in the IO field, a huge level of unmet need remains. High-prescribing physicians surveyed by GlobalData across eight major markets (8MM: US, France, Germany, Italy, Spain, UK, Japan, and China) identified a broad range of unmet needs in the IO space (see Figure 1).

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Pharmaceutical Technology

SEPTEMBER 30, 2022

Spark Therapeutics’ Luxturna, indicated for inherited retinal disease (IRD), was the first gene therapy to be approved, in 2017, with a price tag of $850,000 for each eye. As children continue to face this high unmet need, clinicians and families are hopeful that Skysona will be accepted by payers and available for use soon.

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Pharmaceutical Technology

MAY 19, 2023

DMTs for MS have a high price tag, particularly in the US. KOLs believe that there is a large unmet need for curative therapies in MS, especially for agents that could stop the progress of neurodegeneration such as remyelination therapies, of which there are several in early-stage development.

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pharmaphorum

JANUARY 11, 2022

. “The advancement of innovative therapeutic options for the treatment of the associated distress that often follows a diagnosis is promising for patients and addresses an unmet need,” said Areej El-Jawahri of Massachusetts General Hospital. The post Blue Note leukaemia DTx gets FDA breakthrough tag appeared first on.

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pharmaphorum

JANUARY 18, 2022

Two Spanish pharma companies are joining forces to identify new oral treatments for immune-inflammatory skin diseases with high unmet medical needs. Almirall and IRB Barcelona (the Institute for Research in Biomedicine), will conduct research using molecular glue degraders, a new approach to the skin diseases under scrutiny.

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pharmaphorum

DECEMBER 23, 2022

But along with strong efficacy come some considerable risks and costs: cytokine release syndrome (CRS), where a patient’s immune system becomes dangerously over-stimulated, and neurotoxicity are potential side effects that need to be managed. Side effects and cost implications.

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pharmaphorum

JUNE 2, 2022

When asked by pharmaphorum why product sales are expected to be so high in this area, a spokesperson for Evaluate explained: “For many rare diseases, there is high unmet need which results in high levels of use of orphan products in the eligible patient groups, and these groups are often larger than anticipated once treatments become available.

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