Pharmaceutical Technology

APRIL 5, 2023

But access to these treatments continues to remain limited due to high price tags and variable availability across regions. And my estimate is that between 25,000 and 30,000 patients have been treated with those therapies globally, which does not include patients treated in clinical trials. How has the field changed in recent years?

FDA 59

FDA Immunization 59

Pharmaceutical Technology

JUNE 21, 2023

The high price tag may be hard to defend , but with lifetime treatment costs for haemophilia B reaching as high as $23m for some, the single-dose treatment could prove far more cost-effective. Already a big player in haemophilia treatments, CSL licensed exclusive global rights to Hemgenix from gene therapy developers uniQure back in 2021.

FDA 98

FDA 98

ISPE

JANUARY 9, 2023

For example, based on benchmarking different cases, inserting four additional data points as tags into an existing data store would require an entire week of IT and QA collaboration. An increase in computing power requirements for AI model training brings a higher price tag, so careful planning is necessary to avoid surprises.

Documentation 52

Documentation Communication 52