Remove tag birth-tissue
article thumbnail

Second unanimous FDA adcomm vote boosts bluebird bio

pharmaphorum

Thursday saw the Cellular, Tissue and Gene Therapies advisory committee back elivaldogene autotemcel (eli-cel) for cerebral adrenoleukodystrophy (CALD) – see our report here – and the following day it was the turn of betibeglogene autotemcel (beti-cel) for beta thalassaemia.

FDA 59