Fri.Feb 21, 2025

article thumbnail

First-in-human data for gene therapy signals potential in childhood blindness

European Pharmaceutical Review

New clinical research from the UK has revealed the significant potential of a gene therapy to treat young children with AIPL1-related retinal dystrophy. Findings of the first-in-human study, published in The Lancet , reported that the four children with the rare genetic deficiency benefited substantially, as they gained strong improvements in their eyesight.

article thumbnail

STAT+: Maryland lawmakers vote to expand powers of the state’s prescription drug affordability board

STAT

The Maryland House of Delegates has voted overwhelmingly to allow a state board to extend its mandate for lowering prescription drug costs to all residents, not just those employed by government agencies. As a result, the initiative now goes to the state senate for approval, although the timing is unclear. Nonetheless, the 98-to-34 vote was cheered by consumer advocates who hope the Prescription Drug Affordability Board, which is designed to function much like a state utility commission, will us

Insiders

Sign Up for our Newsletter

This site is protected by reCAPTCHA and the Google Privacy Policy and Terms of Service apply.

article thumbnail

Creative Biolabs Continues Partnering with Pharmaceutical Corporations to Drive Biopharmaceutical Innovation for 2025 and Beyond

Pharma Mirror

As a provider of custom services, Creative Biolabs aims to support the entire process of drug discovery and development for the global pharmaceutical industry using its cutting-edge technology and wide-ranging experiences. It is no secret that the complexities associated with biopharmaceuticals are ever increasing, particularly regarding the development of antibody therapeutics.

article thumbnail

Texas Health Department Investigating Measles Outbreak as Case Count Reaches 90

Drug Topics

Measles is highly contagious, and the Texas Department of State Health Services said that additional cases are likely to occur in Gaines County, which had 57 cases as of February 21, 2025.

article thumbnail

From Diagnosis to Delivery: How AI is Revolutionizing the Patient Experience

Speaker: Simran Kaur, Founder & CEO at Tattva Health Inc.

The healthcare landscape is being revolutionized by AI and cutting-edge digital technologies, reshaping how patients receive care and interact with providers. In this webinar led by Simran Kaur, we will explore how AI-driven solutions are enhancing patient communication, improving care quality, and empowering preventive and predictive medicine. You'll also learn how AI is streamlining healthcare processes, helping providers offer more efficient, personalized care and enabling faster, data-driven

article thumbnail

In FDA job cuts, experts see threat of far-reaching impact

PharmaVoice

"Any place that gets cut, it's going to have an impact, because there's not any spare personnel at FDA,” said former agency commissioner Robert Califf, of the layoffs.

FDA
article thumbnail

Mental Health First Aid Training Can Help Pharmacists Provide Better Care

Drug Topics

Pharmacists who participated in the mental health first aid training had better understanding of mental health conditions and increased confidence and skills in mental health intervention.

More Trending

article thumbnail

FDA Approves Chenodiol for Treatment of Cerebrotendinous Xanthomatosis

Drug Topics

Ctexli is the first FDA-approved treatment for adults with cerebrotendinous xanthomatosis.

FDA
article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

Congress and state leaders must resist short-term cost-cutting measures that cause long-term harm, create cycles of poverty and dismantle the middle class.

article thumbnail

Q&A: Innovative Technologies Revolutionizing Pain Medicine

Drug Topics

Physician with expertise in pain research discussed emerging technologies in the future of pain medicine and how they must be adapted to improve patient outcomes.

article thumbnail

A Common Blood Pressure Medication May Help Treat Symptoms of ADHD

Pharmacy Times

In a study of 5 different drugs, amlodipine was the only one to reduce hyperactivity in patients with attention-deficit hyperactivity disorder (ADHD).

article thumbnail

Position Your Pharmacy for Expansion

Speaker: Chris Antypas and Josh Halladay

Access to limited distribution drugs and payer contracts are key to pharmacy expansion. But how do you prepare your operations to take the next step? Meaningful data: Collect and share clinical data regarding outcomes, utilization, and more Reporting: Limited distribution models require efficient tracking and reporting systems Workflows: Align workflows with specific pharma and payer contractual requirements For in-depth, expert insights on pharmacy expansion, watch this webinar from Inovalon.

article thumbnail

FDA Says Ozempic, Wegovy Shortage Resolved

Drug Topics

Semaglutide has been in shortage since 2022 due to increased demand.

FDA
article thumbnail

Could housecats act as a vector to spread the H5N1 virus?

STAT

Get your daily dose of health and medicine every weekday with STAT’s free newsletter Morning Rounds.  Sign up here. I’m back after a two-week India trip, but mentally I am still scrambling up slopes in the Himalayan foothills. Please send your favorite chai recipes.

article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

The Department of Justice is probing UnitedHealth Group's billing practices in Medicare Advantage, according to a report from the Wall Street Journal.

article thumbnail

Intestinal Microbiome May Play a Role in CAR T-Cell Therapy Outcomes

Pharmacy Times

Melody Smith, MD, MS, discusses how the intestinal microbiome influences CAR T-cell therapy outcomes, highlighting the negative impact of certain antibiotics and the potential role of dietary interventions in improving treatment efficacy.

article thumbnail

What the FDA's New Dosage Guidance Means for the Future of Clinical Research

Speaker: Dr. Ben Locwin - Biopharmaceutical Executive & Healthcare Futurist

What will the future hold for clinical research? A recent draft from the FDA provides valuable insight. In "Optimizing the Dosage of Human Prescription Drugs and Biological Products for the Treatment of Oncologic Diseases," the FDA notes that "targeted therapies demonstrate different dose-response relationships compared to cytotoxic chemotherapy, such that doses below the Maximum Tolerated Dose (MTD) may have similar efficacy to the MTD but with fewer toxicities.

article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

The AI agents have access to a 360-degree view of patient information drawn from unified clinical and claims data and can handle tasks such as scheduling, follow-ups and care coordination.

article thumbnail

Engineered Fat Cells Starve Cancer and Slow Tumor Growth

Pharmacy Times

The approach targets cancer glucose and fatty acid metabolism, which is essential for cancer cell growth.

article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

Staffing difficulties and population growth will cut down the number of open acute care hospital beds over the next decade should hospitalization rates and other trends remain unchanged, new projections show.

article thumbnail

Pfizer shelves haemophilia gene therapy Beqvez amid low demand

Pharmaceutical Technology

Pfizer said resources will be directed to its other haemophilia gene therapy Hympavzi.

article thumbnail

5 Reasons to Upgrade Your Pharmacy Management Software

Are you still using workarounds to manage your daily operations? To achieve peak performance, it's time to explore other options for specialty and infusion pharmacy software. Streamline pharmacy operations and improve clinical performance with automated processing, real-time data exchange, and electronic decision support. Download this helpful infographic to: Drive efficiency and patient adherence from referral receipt to delivery and ongoing care – all with our Pharmacy Cloud.

article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

CVS Health's MinuteClinic and Georgia-based Emory Healthcare are expanding their partnership to provide in-network primary care services at the retail clinics.

article thumbnail

Chenodiol, First Treatment for Cerebrotendinous Xanthomatosis, Receives FDA Approval

Pharmacy Times

This marks the first treatment to be FDA-approved for this rare lipid storage disease.

FDA
article thumbnail

Poolbeg slumps as Hookipa merger is called off

pharmaphorum

A proposed merger of the UK's Poolbeg with Austrian biotech Hookipa has been called off after the latter abruptly withdrew from negotiations.

article thumbnail

Key Sessions and Opportunities for Pharmacists at the AACR Immunotherapy Conference

Pharmacy Times

The AACR Immunotherapy Conference 2025 will provide pharmacists with the opportunity to engage with cutting-edge cancer immunotherapy research, explore advancements in treatments, such as immune checkpoint inhibitors and CAR T-cell therapy, and connect with key leaders in the field.

article thumbnail

Cell therapies are the future of healthcare, why are we struggling to make them at scale?

pharmaphorum

Cell therapies show great promise for revolutionising healthcare, but challenges remain in scaling up production. Learn more about the current obstacles and potential solutions in this informative article.

article thumbnail

FDA Grants Breakthrough Therapy Designation to SkinTE for Diabetic Foot Ulcers

Pharmacy Times

SkinTE could aid Wagner grade 1 diabetic foot ulcers by regenerating and activating the tissues surrounding the wound to heal it completely.

FDA
article thumbnail

AstraZeneca builds in China as Cosette buys Mayne

pharmaphorum

The reporting week has ended with a flurry of M&A as Cosette Pharma and AstraZeneca agree takeover deals

article thumbnail

Weekly Mim8 Effective in Pediatric Hemophilia A With and Without Inhibitors

Pharmacy Times

The new data demonstrates the effectiveness of Mim8 in children with hemophilia A regardless of inhibitor status, expanding the populations in which the novel drug in development could have a treatment benefit.

article thumbnail

The Biosimilars Landscape Through the Eyes of an Economist

Pharmaceutical Commerce

James D. Chambers, PhD, MPharm, MSc, professor of medicine at the Tufts Medical Center Institute for Clinical Research and Health Policy Studies, dives into why biosimilars contribute to a reduction in cost and increase in patient access, while highlighting challenges to adoption.

article thumbnail

Trial of Boehringer's cystic fibrosis gene therapy imminent

pharmaphorum

Boehringer's cystic fibrosis gene therapy is poised to start clinical testing, hoping to offer a one-shot alternative to costly CFTR modulator drugs.

article thumbnail

Fierce Healthcare - Untitled Article

Fierce Healthcare

Millie plans to expand its footprint and add more services, fueled by a $12 million series A funding round. The company will soon open its second clinic in San Francisco's South Bay in collaboration with Good Samaritan Hospital, part of HCA Healthcare.

article thumbnail

Administering Plasma Therapy Requires Pharmacist Collaboration With Specialty Care Team

Pharmacy Times

Plasma therapy can involve burdensome procedures and infusions for patients, but pharmacists can use their expertise to make the process easier and more convenient.

article thumbnail

GLP-1 receptor agonists could hold promise for opioid use disorder treatment

Pharmaceutical Technology

Glucagon-like peptide-1 receptor agonists (GLP-1RAs), originally developed for treating diabetes, work by stimulating insulin secretion and suppressing glucagon release, thereby helping regulate blood sugar.

article thumbnail

Chromosome Genomic Array Testing Improves Myelofibrosis Prognostication for Patients Undergoing Transplantation

Pharmacy Times

Using chromosome genomic array testing in combination with existing risk stratification models can better determine patients with myelofibrosis who can benefit from transplant.

article thumbnail

Struggling bluebird bio to go private for less than $30m

Pharmaceutical Technology

Bluebird has faced financial pressures over the last few years, leading to several restructuring efforts.